Gene therapy platform targeting rare metabolic disorders using CRISPR base-editing.
Melbourne·Trust score 81 / 100·Domain age 19 mo
About
Ember Therapeutics emerged from Monash University's biotech incubator with proprietary base-editing techniques that reduce off-target effects in rare disease treatment. The team has published in top-tier journals and secured partnerships with major pharmaceutical CROs. They're currently conducting preclinical studies on three lead candidates.